Johns Hopkins researchers along with academic and drug industry investigators say they have identified a new biological target for treating spinal muscular atrophy. (sciencedaily.com)
«Promising new drug could help treat spinal muscular atrophy.» (sciencedaily.com)
April 24 - Drugmaker Biogen Inc's quarterly revenue missed analysts» estimates on Tuesday as it had disappointing sales of its promising drug Spinraza to treat spinal muscular atrophy because fewer new patients used the expensive treatment. (cnbc.com)