The Boston startup said its deal with the New York - based Spinal Muscular Atrophy Foundation calls for two years of research and development funding from the foundation. (smafoundation.org)
Spinraza, the first Food and Drug Administration - approved treatment for spinal muscular atrophy, had quarterly... (cnbc.com)
Healthy mice will rear about six times, mice with spinal muscular atrophy treated with both therapies reared about four times and mice with either drug alone only reared about two times. (sciencedaily.com)